Researchers from McMaster University and the Icahn School of Medicine at Mount Sinai, New York have discovered that a protein associated with neurodegenerative diseases like ALS also plays an…
Tag: Muscular Dystrophy / ALS
In Mice With Myotonic Dystrophy, Drug Delivery Strategy Eliminates Myotonia Symptoms
By targeting the specific mutation that causes the hereditary neuromuscular disease myotonic dystrophy, it is possible to neutralize the mutant RNA toxicity and minimize or even eliminate the disabling symptoms of the disease. New classes of drugs cal…