SEVILLE, Spain — Gene therapy is an area of intensive research and development in the retina space, with promising prospects and significant challenges.
The benefits and pitfalls of gene therapy were discussed by two specialists at the Congress on Controversies in Ophthalmology.
Luis Arias, MD, PhD, described the different methods of gene therapy — gene addition, gene editing and RNA therapy — and vector systems, of which the adeno-associated virus is the most commonly used.
“Ocular diseases are a focus for gene therapy due to the accessibility and isolation, the