AGTC’s retinitis pigmentosa gene therapy candidate shows positive 6-month results

An adeno-associated virus-based gene therapy improved visual function in patients with X-linked retinitis pigmentosa 6 months after dosing, Applied Genetic Technologies Corporation announced in a press release.
Secondary data from a phase 1/2 clinical trial showed a favorable safety profile in all 25 patients treated with the AAV-based gene therapy product candidate. Patients treated centrally showed durable improvement in visual function.
“These promising results further demonstrate that our XLRP candidate has tremendous potential to provide meaningful benefit to XLRP patients who today

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