Retinal sensitivity improved in patients with RPGR-associated X-linked retinitis pigmentosa treated with an AAV-RPGR gene therapy, a speaker said at the virtual American Society of Retina Specialists meeting.
“In our low- and intermediate-dose cohorts, we have achieved clinically meaningful improvements in retinal sensitivity across multiple metrics and modalities,” Michel Michaelides, BSc, MB BS, MD(Res), FRCOphth, FACS, said.
Because of their good safety profile, the low and intermediate doses are being taken forward in the ongoing randomized controlled dose-expansion phase of the
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